X-Message-Number: 9621 Date: Tue, 5 May 1998 02:24:29 -0400 From: Mike Darwin <> Subject: 21CM Cerebral Resuscitation Saul Kent has asked me to briefly outline the cerebral resuscitation and critical care medicine research 21st Century Medicine (21CM) is doing. I do not think this is the appropriate venue for detailed disclosures and, as we are pursuing both patent protection and peer-reviewed publication of this work, I will keep my remarks general. A few days ago anyone not living under a freeway underpass in the United States became aware that the FDA had approved a pill to treat impotence (Viagra) which appears to be highly effective and which in pre-launch studies, of which the FDA was aware,appeared to facilitate intercourse in most post-pubertal males_and females_ (not just in the target population of 50+ yr old males). Viagra now accounts for 2 of every 3 prescriptions being written in the US. Yesterday, Bob Ettinger posted a summary of a news-service story describing the incredible success of angiostatin and endostanin in "curing" virtually all solid tumors in rodents and quoted the researchers as having even more optimistic data than has yet been published. To my knowledge this true; this drug combination has worked in three species so far and has shown minimal side effects and virtually complete efficacy against all solid tumors on which it has been tried (adenocarcinomas, sarcomas, osteosarcomas and several others). To put this into perspective, adenocarcinomas alone constitute the vast majority of solid tumors of clinical relevance and human terror: cancers of the lung, breast, mouth, stomach colon, anus/rectum, and pancreas. Similarly, the statin-drugs (such Lovastatin) have been shown to cut cardiovascular morbidity and mortality by 50% if started in persons at risk of a heart attack even in middle age and to similarly reduce mortality in patients who have suffered a first heart attack (i.e., reducing their likelihood of dying of a second heart attack). Finally, the protease inhibitors and combination antiviral therapy have emptied out hospices and closed down virtually every AIDS unit in Southern California in the space of 18 months. All this and Prozac too! The purpose of the above rather lengthily paragraph is to point out that we live in interesting times and that the century ahead (if we don't destroy ourselves) will be the century of biology, as this, the 20th century has been the century of physics and engineering. One of my primary reasons for becoming involved in human cryopreservation as a 13-year-old was a desire to defeat death and to be a part of the emerging control over every aspect of human biology. In beginning my career in cryonics I began at the beginning: which was the problem of how to maintain the newly "dead" patient in a viable condition, or at least to minimize injury from ischemia as much as possible until definitive stabilization (freezing) could be brought to bear. I naively thought this would be a relatively easy task since extended CPR seemed to fit the bill for what was needed and a few problems such as cold-agglutination, acidosis and anticoagulation could be easily overcome. Now, 30 years later, I have a far different perception. I learned, much to my horror, on the first patient I had the opportunity to begin immediate machine assisted CPR on under ideal conditions (i.e., in hospital within seconds of pronouncement and with an intact circulatory system which had not been ravaged by hours of pre-mortem shock or multi-system organ failure) that closed chest CPR didn't work. My patient went into rigor mortis within a few hours despite excellent mechanical CPR, buffering, anticoagulation, and what was then thought to be adequate external cooling with ice bags. That patient taught me a lot. His name can be disclosed now: it was Willie DeMar. Because I collected enormous amounts of data from that patient and subsequent ones I was able to determine that there were many problems, not the least of which was that it took him nearly 8-hours to cool to just about room temperature! Most of that time I was moving essentially no blood, the patient having gone into rigor within 2 hours after the start of "transport." Watching cryopatients die up-close and personal and having the added opportunity to work in hospital in a critical care setting for the better part of a decade taught me a great deal more. Until recently however, all of the efforts I've exerted have resulted in incremental advances or improvements in the front-end of care (cardiopulmonary-cerebral resuscitation) of patients as opposed to dramatic advances in capability. I learned how to cool patients more rapidly by direct contact with ice and and water and invented the PIB, and with Jerry Leaf, became expert at developing systems that allowed for rapid (by cryonics standards), in-field heart-lung machine facilitated cooling and oxygenation of cryopatients as well as blood washout with extended recovery and survival as a routine expectation (using a dog model for validation). Periodically we would apply our growing insights and technology to ostensibly reversible animal models of sudden cardiac death trying to recover dogs from periods of _normothermic_ cerebral ischemia of 10 to 12 minutes' duration, but with no success. The last 5 years has seen an explosion in our understanding in the pathophysiology of ischemic injury: We are now beginning to understand the critical biochemical and biophysical events that cause injury and prevent long-term recovery of dogs (and people) after periods of cardiac arrest of much greater than 6 minutes duration. Equally important, via the modality of liquid perfluorochemical ventilation I have learned how to _rapidly_ cool patients by the crtitical 2 degrees necessary to facilitate cerebral preservation upon reperfusion (restart of blood circulation). Just as importantly, a virtual cornucopia of drugs and bio-regulatory molecules are becoming available to us to block many if not all of the critical damaging reactions that occur during both ischemia and upon reperfusion. At 21CM we early on adopted a philosophy that cerebral ischemia-reperfusion injury was complex, multifactorial and that a single magic bullet mon-drug or approach was unlikely to work. We carefully studied the literature and observed that with few exceptions, virtually all of the work being done in this area was done using small animal models with a mono-therapeutic approach. The reasons for this are many and I will list but a few: *Drug combinations are rarely, if ever approved by the U.S. FDA. *Most institutional research is aimed at unraveling the mechanics of a particular aspect of the pathology with the endpoint being a measured biochemical, physiological, or behavioral parameter. For example, a single free radical blocking drug might be given to determine the importance of free radicals in ischemic injury of a high specialized kind with the measured end-point being detection of free radical inhibition in brain tissue upon reperfusion by a measurement such as chemiluminesence. *Multi-modal therapeutic research is costly and difficult to conduct and creates great problems in determining exactly _what_ part of the protocol is working. *The few multimodal trials done to date have usually shown a net negative benefit to combining drugs. *For the above reasons it is difficult to publish papers using such approaches in peer-reviewed journals which focus on "clean" science with a strong emphasis on understanding small parts of the problem definitively. *Most of this work is done by people who get rewarded for a "nice" piece of science rather than a definitive clinical endpoint. This last point is very important, and I'll get to it directly. At 21CM our goal was not _primarily_ to further understanding into the mechanics of injury in ischemia, but rather to overcome ischemic injury. Our endpoint was not reducing the evidence of histological damage, or the level of key biochemical markers of injury, but rather to achieve integrated, long term survival of animals _without neurological deficit_ in a model directly relevant to humans. We spent a great deal of time and money choosing, developing, and validating the model. We also spent a great deal of time and energy trying to sift through the enormous literature on cerebral ischemia-reperfusion injury and come to some conclusions about what were the most important mechanisms and pathways of injury to treat or block and which were the best, least expensive, most readily available drugs to achieve these ends with. Our sole mission was to get dogs back with reasonable consistency after 15 to 20 minutes of normothermic cardiac arrest (whole body ischemia at 37.5 C) and _without neurological deficit._ In others words; the dogs had to survive, recover fully, and show retention of memory as well as the ability to learn and interact socially with humans normally. (The latter is a dauntingly complex task requiring full conservation of mentation). The structure of this kind of research approach is technologically oriented rather than academic. It is a "moonshot" mentality rather than a "doctoral dissertation" mentality. This is _not_ to slight the thousands of toiling scientists working on mono-modal treatments and teasing out basic biological pathways of injury: these people made our work possible. And, quite podssibly, some of them _will_ discover magic bullet drugs with enormous payoff. What we have done is to use a complex, multi-drug cocktail to treat cerebral ischemia-reperfusion injury. We have further learned that in addition to drugs there must be artificial, _automated_ re-imposition of physiological "homeostasis," or regulation of the animal's internal environment for a period of some hours following resuscitation. We have further discovered that the complexity and possible adverse interaction of the drugs used in the protocol requires computer driven AI algorithms to control timing, sequence, and the amount of various drugs delivered. In short, drugs alone are not enough, an integrated system which measures multiple critical physiological parameters inside the animal and then _adjusts_ them optimally with both pharmacological and mechanical interventions is critical to success. Using this approach we have achieved in the pilot canine cerebral resuscitation experimental group: 100% acute neurological recovery following 15 to 17 minutes of total body cardiac arrest at 37.5 C. 75% long term-survival of animals (i.e., great than 1 month) with normal kennel behavior (i.e., motor function, grooming, reproduction, etc). 50% of survival animals have no detectable neurological deficit with complex behavioral evaluation (including learning and memory). 50% survival of animals with _mild_ neurological deficit: subtle changes in ability to learn or remember or behavior changes such decreased inhibition and loss of social interactivity with humans. There has been 100% mortality in the control group. There has been 100% lack of acute neurological recovery in our historical controls using the typical American Heart Association Advanced Cardiac Life Support (ACLS) Protocol. The longest we have recovered a dog from normothermic cardiac arrest is 17 minutes, with normal mentation at 3 months post-procedure. We are now in the process of locking our protocol into place and beginning a fully blinded statistical run with a standardized insult time of 15 minutes of cardiac arrest. The relevance of this work to contemporary medicine is potentially enormous. In the United States approximately 350,000 people die each year from failed cerebral resuscitation. Many others die or suffer lasting disability from head trauma, and one thing we have learned at 21CM is much of the pathophysiology of blunt force head trauma overlaps that of ischemia-reperfusion injury. The company has no plans to directly market this technology, but rather to pursue licensing in order to generate revenues. The company also has no plans to conduct clinical trials in the U.S. or to introduce this technology to the U.S. marketplace, even though the U.S. constitutes 2/3rds of the world's overall drug market. It is also fair to say that this work is in its infancy with enormous amounts of hardware and software development needed to facilitate optimum application of our protocol. Some of the drugs used in our protocol are novel and patentable and will be of direct, and we believe, potent therapeutic utility as stand- alone molecules used to treat specific critical illnesses such as shock, malignant hyperthermia, heat stroke, and post-traumatic respiratory distress syndrome. Others are the products of other pharmaceutical companies. One of the frustrating and exciting things about this work is that we have scarcely scratched the surface of the possibilities. We are achieving what we believe to be astonishing results now, and yet we have over 40 novel compounds which we currently do not have the resources to evaluate, but which offer the promise of even better results both in terms of outcomes at the current time limit of 17 minutes, and in terms of allowing recovery from longer arrest periods, perhaps out to as long as 30 to (in selected cases) 60 minutes of clinical death at normothermia without neurological deficit. Recently Bob Ettinger and the Cryonics Institute criticized the 21CM cerebral resuscitation research program stating: >some of us have problems with infliction of suffering on dogs or >other animals, even if the eventual goal is to save human life. Certainly this >is a gray area, but I want it on the record, again, that Cryonics Institute >does no experiments on live animals. When they are killed for our research, it >is either routinely at a slaughterhouse where it would have happened in any >event, or by euthanasia under the supervision of a veterinarian, and not on CI >premises in any case. I will have more to say on this soon. It is sufficient to say now that animals in our laboratory are managed for pain and discomfort using the best available pharmaceutical technology with cost as no barrier, including the use of drugs such as Propofol which allow for titration of sedation and, when coupled with morphine and or Fentanyl, (we have a DEA license) allow for very tight control over pain and agitation. It is certainly the case that our our animals are managed for post-operative pain and discomfort better than the millions of companion animals (pets) who undergo painful surgical procedures and then are caged or sent home with their owners with NO pain management whatsoever. In summary, we believe that our work has the potential to improve the quality and length of both human and companion animal life and we feel our work is very worthwhile. We see the company's prospects for financial rewards in this area with caution. There are many obstacles to successful clinical application of this technology. Personally, I believe the real profit centers at 21CM are likely to be vastly improved cryopreservation methods with application not just to transplantation but to engineered tissues and to conventional cryopreservation technologies, perhaps allowing, for instance, stable dry ice temperature storage of viable cells and tissues such sperm, ova, embryos and blood: thus eliminating the need for costly and dangerous technologies such as liquid nitrogen storage and superinsulated dewars for transportation of cryopreserved biologicals. Nevertheless, the company maintains a strong commitment to critical care medicine and some of the first human clinical applications of 21CM technology seem likely to come from that division of the company. Mike Darwin, Director of Research 21st Century Medicine Rate This Message: http://www.cryonet.org/cgi-bin/rate.cgi?msg=9621